CRISPR/Cas9 mediated gene correction ameliorates abnormal phenotypes in spinocerebellar ataxia type 3 patient-derived induced pluripotent stem cells

por He, Lang, Wang, Shang, Peng, Linliu, Zhao, Huifang, Li, Shuai, Han, Xiaobo, Habimana, Jean de Dieu, Chen, Zhao, Wang, Chunrong, Peng, Yun, Peng, Huirong, Xie, Yue, Lei, Lijing, Deng, Qi, Wan, Linlin, Wan, Na, Yuan, Hongyu, Gong, Yiqing, Zou, Guangdong, Li, Zhiyuan, Tang, Beisha, Jiang, Hong
Publicado 2021

The Natural History of Spinocerebellar Ataxia Type 3 in Mainland China: A 2-Year Cohort Study

por Peng, Yun, Peng, Linliu, Chen, Zhao, Peng, Huirong, Wang, Puzhi, Zhang, Youming, Li, Yangping, Wang, Chunrong, Shi, Yuting, Hou, Xuan, Long, Zhe, Yuan, Hongyu, Wan, Na, Wan, Linlin, Xu, Keqin, Lei, Lijing, Wang, Shang, He, Lang, Xie, Yue, Gong, Yiqing, Deng, Qi, Zou, Guangdong, Tang, Zhichao, Shen, Lu, Xia, Kun, Qiu, Rong, Klockgether, Thomas, Tang, Beisha, Jiang, Hong
Publicado 2022