Efficacy and long term safety of alipogene tiparvovec (AAV1-LPL(S447X)) gene therapy for lipoprotein lipase deficiency: an open label trial

por Gaudet, Daniel, Méthot, Julie, Déry, Stéphane, Brisson, Diane, Essiembre, Christiane, Tremblay, Gérald, Tremblay, Karine, de Wal, Janneke, Twisk, Jaap, van den Bulk, Nick, Sier-Ferreira, Valerie, van Deventer, Sander
Publicado 2012