A pediatric quantitative systems pharmacology model of neurofilament trafficking in spinal muscular atrophy treated with the antisense oligonucleotide nusinersen

por Paris, Alessio, Bora, Pranami, Parolo, Silvia, MacCannell, Drew, Monine, Michael, van der Munnik, Nick, Tong, Xiao, Eraly, Satish, Berger, Zdenek, Graham, Danielle, Ferguson, Toby, Domenici, Enrico, Nestorov, Ivan, Marchetti, Luca
Publicado 2022