Goal attainment scaling as an outcome measure in rare disease trials: a conceptual proposal for validation

por Gaasterland, C. M. W., van der Weide, M. C. Jansen, Roes, K. C. B., van der Lee, J. H.
Publicado 2019

The patient’s view on rare disease trial design – a qualitative study

por Gaasterland, C. M. W., van der Weide, M. C. Jansen –, du Prie – Olthof, M. J., Donk, M., Kaatee, M. M., Kaczmarek, R., Lavery, C., Leeson-Beevers, K., O’Neill, N., Timmis, O., van Nederveen, V., Vroom, E., van der Lee, J. H.
Publicado 2019