Registries for orphan drugs: generating evidence or marketing tools?

por Hollak, Carla E. M., Sirrs, Sandra, van den Berg, Sibren, van der Wel, Vincent, Langeveld, Mirjam, Dekker, Hanka, Lachmann, Robin, de Visser, Saco J.
Publicado 2020

Effectiveness and safety of mexiletine in patients at risk for (recurrent) ventricular arrhythmias: a systematic review

por van der Ree, Martijn H, van Dussen, Laura, Rosenberg, Noa, Stolwijk, Nina, van den Berg, Sibren, van der Wel, Vincent, Jacobs, Bart A W, Wilde, Arthur A M, Hollak, Carla E M, Postema, Pieter G
Publicado 2022

A novel sustained‐release cysteamine bitartrate formulation for the treatment of cystinosis: Pharmacokinetics and safety in healthy male volunteers

por Berends, Cécile L., Pagan, Lisa, van Esdonk, Michiel J., Klarenbeek, Naomi B., Bergmann, Kirsten R., Moerland, Matthijs, van der Wel, Vincent, de Visser, Saco J., Büller, Hans, de Loos, Frans, de Vries, Wouter S., Waals, Hans, de Leede, Leo G. J., Burggraaf, Jacobus, Kamerling, Ingrid M. C.
Publicado 2021