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Access to medicines for rare diseases: A European regulatory roadmap for academia
Background: Novel or repurposed medicines for rare diseases often emerge from fundamental research or empirical findings in academia. However, researchers may be insufficiently aware of the possibilities and requirements to bring novel medicinal treatment options to the patient. This paper aims to p...
Autores principales: | Rosenberg, Noa, van den Berg, Sibren, Stolwijk, Nina N., Jacobs, Bart A. W., Post, Hendrika C., Pasmooij, Anna M. G., de Visser, Saco J., Hollak, Carla E. M. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10012277/ https://www.ncbi.nlm.nih.gov/pubmed/36925633 http://dx.doi.org/10.3389/fphar.2023.1142351 |
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