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Recent Trends in Antisense Therapies for Duchenne Muscular Dystrophy
Duchenne muscular dystrophy (DMD) is a debilitating and fatal genetic disease affecting 1/5000 boys globally, characterized by progressive muscle breakdown and eventual death, with an average lifespan in the mid–late twenties. While no cure yet exists for DMD, gene and antisense therapies have been...
| Autores principales: | , |
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| Formato: | Online Artículo Texto |
| Lenguaje: | English |
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MDPI
2023
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| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10054484/ https://www.ncbi.nlm.nih.gov/pubmed/36986639 http://dx.doi.org/10.3390/pharmaceutics15030778 |