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Top Caregiver Concerns in Rett syndrome and related disorders: data from the US Natural History Study

OBJECTIVE: Recent advances in the understanding of neurodevelopmental disorders such as Rett syndrome (RTT) has enabled development of novel therapeutic approaches that are currently undergoing clinical evaluation or are proposed to move into clinical development. Clinical trial success depends on o...

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Detalles Bibliográficos
Autores principales: Neul, Jeffrey Lorenz, Benke, Timothy A., Marsh, Eric D., Suter, Bernhard, Silveira, Lori, Fu, Cary, Peters, Sarika U., Percy, Alan K.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Journal Experts 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10055548/
https://www.ncbi.nlm.nih.gov/pubmed/36993737
http://dx.doi.org/10.21203/rs.3.rs-2566253/v1