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Epidemiology and patient journey of Rett syndrome in the United States: a real-world evidence study

BACKGROUND: Rett syndrome (RTT) is a neurodevelopmental disorder that almost exclusively affects females and is associated with high clinical burden. However, literature characterizing the real-world journey of patients with RTT is limited. This study provided an overview of the epidemiology, patien...

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Detalles Bibliográficos
Autores principales:	May, Damian, Kponee-Shovein, Kalé, Mahendran, Malena, Downes, Nathaniel, Sheng, Kristy, Lefebvre, Patrick, Cheng, Wendy Y.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2023
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10071755/ https://www.ncbi.nlm.nih.gov/pubmed/37016355 http://dx.doi.org/10.1186/s12883-023-03181-y

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