Cargando…
A model for crowdsourcing high-impact research questions for Castleman disease and other rare diseases
BACKGROUND: There are approximately 10,000 rare diseases that affect around 30,000,000 individuals in the U.S.A., most of which do not have an FDA-approved treatment. This fact highlights the failure of traditional research approaches to overcome the unique challenges of developing rare disease trea...
Autores principales: | Korsunska, Ania, Repasky, Mileva, Zuccato, Mary, Fajgenbaum, David C. |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2023
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10091676/ https://www.ncbi.nlm.nih.gov/pubmed/37041585 http://dx.doi.org/10.1186/s13023-023-02678-6 |
Ejemplares similares
-
Taking Control of Castleman Disease: Leveraging Precision Medicine Technologies to Accelerate Rare Disease Research
por: Newman, Samantha Kass, et al.
Publicado: (2015) -
The lymph node transcriptome of unicentric and idiopathic multicentric Castleman disease
por: Horna, Pedro, et al.
Publicado: (2022) -
The disease course of Castleman disease patients with fatal outcomes in the ACCELERATE registry
por: Fajgenbaum, David C., et al.
Publicado: (2022) -
PB2708: SYMPTOM BURDEN AND ITS IMPACT ON DAILY LIFE IN PATIENTS WITH IDIOPATHIC MULTICENTRIC CASTLEMAN’S DISEASE (IMCD): AN EXPLORATORY ANALYSIS OF THE SURVEY’S INTERNAL CONSTRUCT VALIDITY
por: Franklin, Matt, et al.
Publicado: (2023) -
AA amyloidosis associated with Castleman disease: A case report and review of the literature
por: Bernabei, Luca, et al.
Publicado: (2020)