Cargando…

Parents’ Experience of Administering Vosoritide: A Daily Injectable for Children with Achondroplasia

INTRODUCTION: Vosoritide is the first approved pharmacological treatment for achondroplasia and is indicated for at-home injectable administration by a trained caregiver. This research aimed to explore parents’ and children’s experience of initiating vosoritide and administering this treatment at ho...

Descripción completa

Detalles Bibliográficos
Autores principales:	NiMhurchadha, Sinead, Butler, Karen, Argent, Rob, Palm, Katja, Baujat, Genevieve, Cormier-Daire, Valerie, Mohnike, Klaus
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Healthcare 2023
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10129947/ https://www.ncbi.nlm.nih.gov/pubmed/37017912 http://dx.doi.org/10.1007/s12325-023-02496-z

Ejemplares similares

Pharmacokinetics and Exposure–Response of Vosoritide in Children with Achondroplasia
por: Chan, Ming Liang, et al.
Publicado: (2021)

Literature review and expert opinion on the impact of achondroplasia on medical complications and health-related quality of life and expectations for long-term impact of vosoritide: a modified Delphi study
por: Savarirayan, Ravi, et al.
Publicado: (2022)

SAT-LB18 A Randomized Controlled Trial of Vosoritide in Children With Achondroplasia
por: Savarirayan, Ravi, et al.
Publicado: (2020)

LBMON196 A Randomized Controlled Trial Of Vosoritide In Infants And Toddlers With Achondroplasia
por: Savarirayan, Ravi, et al.
Publicado: (2022)

Evidence of feedback regulation of C-type natriuretic peptide during Vosoritide therapy in Achondroplasia
por: Prickett, Timothy C. R., et al.
Publicado: (2021)

Lumbar spinal stenosis and disc alterations affect the upper lumbar spine in adults with achondroplasia
por: Huet, Thomas, et al.
Publicado: (2020)

European Achondroplasia Forum guiding principles for the detection and management of foramen magnum stenosis
por: Irving, Melita, et al.
Publicado: (2023)

Optimising the diagnosis and referral of achondroplasia in Europe: European Achondroplasia Forum best practice recommendations
por: Cormier-Daire, Valerie, et al.
Publicado: (2022)

Persistent and Stable Growth Promoting Effects of Vosoritide in Children With Achondroplasia for up to 2 Years: Results From the Ongoing Phase 3 Extension Study
por: Savarirayan, Ravi, et al.
Publicado: (2021)

Safe and persistent growth-promoting effects of vosoritide in children with achondroplasia: 2-year results from an open-label, phase 3 extension study
por: Savarirayan, Ravi, et al.
Publicado: (2021)

Sotos syndrome
por: Baujat, Geneviève, et al.
Publicado: (2007)

Craniofacial growth and function in achondroplasia: a multimodal 3D study on 15 patients
por: Morice, Anne, et al.
Publicado: (2023)

The first European consensus on principles of management for achondroplasia
por: Cormier-Daire, Valerie, et al.
Publicado: (2021)

Real-world evidence in achondroplasia: considerations for a standardized data set
por: Alanay, Yasemin, et al.
Publicado: (2023)

Optimising care and follow-up of adults with achondroplasia
por: Fredwall, Svein, et al.
Publicado: (2022)

Quality of life of children with achondroplasia and their parents - a German cross-sectional study
por: Witt, Stefanie, et al.
Publicado: (2019)

Abnormal pelvic morphology and high cervical length are responsible for high-risk pregnancies in women displaying achondroplasia
por: Vivanti, Alexandre J., et al.
Publicado: (2016)

Rationale, design, and methods of a randomized, controlled, open-label clinical trial with open-label extension to investigate the safety of vosoritide in infants, and young children with achondroplasia at risk of requiring cervicomedullary decompression surgery
por: Savarirayan, Ravi, et al.
Publicado: (2021)

PSAT103 Qualitative Research in Children with Achondroplasia and Parents of Children with Achondroplasia: Medical Challenges and Impacts
por: Muslimova, Elena, et al.
Publicado: (2022)

Experiences of children and adolescents living with achondroplasia and their caregivers
por: Shediac, Renée, et al.
Publicado: (2022)

Infigratinib in children with achondroplasia: the PROPEL and PROPEL 2 studies
por: Savarirayan, Ravi, et al.
Publicado: (2022)

Achondroplasia
por: Hunter, Richard H.
Publicado: (1933)

Achondroplasia
por: Flemming, Charles E. S.
Publicado: (1899)

OR18-5 A Prospective Clinical Trial of Vosoritide in Selected Genetic Causes of Short Stature
por: Boucher, Kimberly, et al.
Publicado: (2022)

Assessing physical symptoms, daily functioning, and well‐being in children with achondroplasia
por: Pfeiffer, Kathryn M., et al.
Publicado: (2020)

Treatment Goals for Achondroplasia: A Qualitative Study with Parents and Adults
por: McGraw, Sarah A., et al.
Publicado: (2022)

The Antiquity of Achondroplasia
por: Bleyer, Adrirn
Publicado: (1940)

Assessing the impacts of having a child with achondroplasia on parent well-being
por: Pfeiffer, Kathryn M., et al.
Publicado: (2020)

Pharmacokinetics and safety after once and twice a day doses of meclizine hydrochloride administered to children with achondroplasia
por: Kitoh, Hiroshi, et al.
Publicado: (2020)

Molecular studies of achondroplasia
por: Nahar, Risha, et al.
Publicado: (2009)

Achondroplasia and periodontal disease
por: Chawla, Kirti, et al.
Publicado: (2012)

Achondroplasia and Macular Coloboma
por: Ahoor, M. H., et al.
Publicado: (2015)

Orofacial manifestations of achondroplasia
por: Rohilla, Smriti, et al.
Publicado: (2012)

Limb lengthening in achondroplasia
por: Chilbule, Sanjay K, et al.
Publicado: (2016)

Correction to: Assessing the impacts of having a child with achondroplasia on parent well-being
por: Pfeiffer, Kathryn M., et al.
Publicado: (2020)

Syndromic forms of congenital hyperinsulinism
por: Zenker, Martin, et al.
Publicado: (2023)

Healthcare trajectory of children with rare bone disease attending pediatric emergency departments
por: Yang, David Dawei, et al.
Publicado: (2020)

PSAT106 Infigratinib in Children with Achondroplasia: Design of the PROPEL, PROPEL2 and PROPEL OLE Studies
por: Muslimova, Elena, et al.
Publicado: (2022)

PSAT105 Evaluation of Body Mass Index and Metabolic Parameters in Children with Achondroplasia Participating in the PROPEL Study
por: Rogoff, Daniela, et al.
Publicado: (2022)

Achondroplasia Associated with Bilateral Keratoconus
por: Al Mahmood, Ammar M., et al.
Publicado: (2012)

Cannot write session to /tmp/vufind_sessions/sess_orfm452ojorrfhk947u1utmoqp