Healthcare Service Use Patterns Among Patients with Acid Sphingomyelinase Deficiency Type B: A Retrospective US Claims Analysis

INTRODUCTION: Acid sphingomyelinase deficiency (ASMD) is a rare lysosomal storage disease. Patients with ASMD type B experience multiple morbidities, potentially leading to early mortality. Before the 2022 approval of olipudase alfa for non-neuronopathic ASMD manifestations, only symptom management...

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Detalles Bibliográficos
Autores principales: Pulikottil-Jacob, Ruth, Ganz, Michael L., Fournier, Marie, Petruski-Ivleva, Natalia
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Springer Healthcare 2023
Materias:
Original Research
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10129952/
https://www.ncbi.nlm.nih.gov/pubmed/36897522
http://dx.doi.org/10.1007/s12325-023-02453-w

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10129952/
https://www.ncbi.nlm.nih.gov/pubmed/36897522
http://dx.doi.org/10.1007/s12325-023-02453-w

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