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Healthcare Service Use Patterns Among Patients with Acid Sphingomyelinase Deficiency Type B: A Retrospective US Claims Analysis

INTRODUCTION: Acid sphingomyelinase deficiency (ASMD) is a rare lysosomal storage disease. Patients with ASMD type B experience multiple morbidities, potentially leading to early mortality. Before the 2022 approval of olipudase alfa for non-neuronopathic ASMD manifestations, only symptom management...

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Detalles Bibliográficos
Autores principales:	Pulikottil-Jacob, Ruth, Ganz, Michael L., Fournier, Marie, Petruski-Ivleva, Natalia
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Healthcare 2023
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10129952/ https://www.ncbi.nlm.nih.gov/pubmed/36897522 http://dx.doi.org/10.1007/s12325-023-02453-w

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