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Neurological Disease Modeling Using Pluripotent and Multipotent Stem Cells: A Key Step towards Understanding and Treating Mucopolysaccharidoses
Despite extensive research, the links between the accumulation of glycosaminoglycans (GAGs) and the clinical features seen in patients suffering from various forms of mucopolysaccharidoses (MPSs) have yet to be further elucidated. This is particularly true for the neuropathology of these disorders;...
Autores principales: | Carvalho, Sofia, Santos, Juliana Inês, Moreira, Luciana, Gonçalves, Mariana, David, Hugo, Matos, Liliana, Encarnação, Marisa, Alves, Sandra, Coutinho, Maria Francisca |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10135551/ https://www.ncbi.nlm.nih.gov/pubmed/37189853 http://dx.doi.org/10.3390/biomedicines11041234 |
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