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Voretigene Neparvovec for the Treatment of RPE65-associated Retinal Dystrophy: Consensus and Recommendations from the Korea RPE65-IRD Consensus Paper Committee

Mutations in the RPE65 gene, associated with Leber congenital amaurosis, early-onset severe retinal dystrophy, and retinitis pigmentosa, gained growing attention since gene therapy for patients with RPE65-associated retinal dystrophy is available in clinical practice. RPE65 gene accounts for a very...

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Detalles Bibliográficos
Autores principales:	Han, Jinu, Joo, Kwangsic, Kim, Ungsoo Samuel, Woo, Se Joon, Lee, Eun Kyoung, Lee, Joo Yong, Park, Tae Kwann, Kim, Sang Jin, Byeon, Suk Ho
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Korean Ophthalmological Society 2023
Materias:	Review Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10151174/ https://www.ncbi.nlm.nih.gov/pubmed/36950921 http://dx.doi.org/10.3341/kjo.2023.0008

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