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The Two Substrate Reduction Therapies for Type 1 Gaucher Disease Are Not Equivalent. Comment on Hughes et al. Switching between Enzyme Replacement Therapies and Substrate Reduction Therapies in Patients with Gaucher Disease: Data from the Gaucher Outcome Survey (GOS). J. Clin. Med. 2022, 11, 5158
Autores principales: | Mistry, Pramod K., Kishnani, Priya S., Balwani, Manisha, Charrow, Joel M., Hull, Judy, Weinreb, Neal J., Cox, Timothy M. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10179580/ https://www.ncbi.nlm.nih.gov/pubmed/37176709 http://dx.doi.org/10.3390/jcm12093269 |
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