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Characteristics of BAY 2599023 in the Current Treatment Landscape of Hemophilia A Gene Therapy

Hemophilia A, a single gene disorder leading to deficient Factor VIII (FVIII), is a suitable candidate for gene therapy. The aspiration is for single administration of a genetic therapy that would allow the production of endogenous FVIII sufficient to restore hemostasis and other biological processe...

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Detalles Bibliográficos
Autores principales:	Pipe, Steven W., Arruda(Late), Valder R., Lange, Claudia, Kitchen, Stephen, Eichler, Hermann, Wadsworth, Samuel
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Bentham Science Publishers 2023
Materias:	Life Sciences, Genetics & Genomics, Molecular Medicine, Genetics & Heredity
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10186383/ https://www.ncbi.nlm.nih.gov/pubmed/36111754 http://dx.doi.org/10.2174/1566523222666220914105729

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