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Real-life impact of highly effective CFTR modulator therapy in children with cystic fibrosis

Introduction: Recently, cystic fibrosis transmembrane regulator modulator therapy with elexacaftor/tezacaftor/ivacaftor has become available for children with cystic fibrosis (CF) carrying at least one F508del mutation. Objective: To assess the intermediate term effects of elexacaftor/tezacaftor/iva...

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Detalles Bibliográficos
Autores principales:	Olivier, Margarete, Kavvalou, Alexandra, Welsner, Matthias, Hirtz, Raphael, Straßburg, Svenja, Sutharsan, Sivagurunathan, Stehling, Florian, Steindor, Mathis
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2023
Materias:	Pharmacology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10203630/ https://www.ncbi.nlm.nih.gov/pubmed/37229253 http://dx.doi.org/10.3389/fphar.2023.1176815

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