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The Metreleptin Effectiveness and Safety Registry (MEASuRE): concept, design and challenges

BACKGROUND: Metreleptin, a recombinant analog of human leptin, is an approved therapy, adjunct to diet, to treat the metabolic complications of leptin deficiency in patients with lipodystrophy – a group of rare diseases characterized by a paucity of adipose tissue. MEASuRE (Metreleptin Effectiveness...

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Detalles Bibliográficos
Autores principales:	Haymond, Morey W, Araújo-Vilar, David, Balser, John, Lewis, James H, Louzado, Ruth, Musso, Carla, von Schnurbein, Julia, Wabitsch, Martin
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2023
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10214317/ https://www.ncbi.nlm.nih.gov/pubmed/37237416 http://dx.doi.org/10.1186/s13023-023-02714-5

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