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Therapeutic potential of fetal liver cell transplantation in hemophilia A mice

Hemophilia A (HA) cell therapy approaches in pediatric individuals require suitable factor (F)VIII-producing cells for stable engraftment. Liver sinusoidal endothelial cells (LSEC) and hematopoietic stem cells (HSC) have been demonstrated to be suitable for the treatment of adult HA mice. However, a...

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Detalles Bibliográficos
Autores principales:	Merlin, Simone, Akula, Saicharan, Cottonaro, Alessia, Garcia-Leal, Tamara, Serrano, Luis Javier, Borroni, Ester, Kalandadze, Vakhtang, Galiano, Rocio, Borsotti, Chiara, Liras, Antonio, Sanchez, María José, Follenzi, Antonia
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Fondazione Ferrata Storti 2023
Materias:	Article - Cell Therapy & Immunotherapy
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10230422/ https://www.ncbi.nlm.nih.gov/pubmed/36700401 http://dx.doi.org/10.3324/haematol.2022.282001

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