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Registry-based study in people with cystic fibrosis and an R117H variant treated with ivacaftor

BACKGROUND: Ivacaftor approval was extended to people with cystic fibrosis (CF) and an R117H variant in 2014 in the USA. This observational, real-world, postapproval study evaluated long-term outcomes among people with CF and an R117H variant on ivacaftor using data from the US Cystic Fibrosis Found...

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Detalles Bibliográficos
Autores principales:	Higgins, Mark, Farietta, Thalia, Campbell, Daniel, Liu, Meng, Ostrenga, Josh, Elbert, Alexander, Shih, Judy, Volkova, Nataliya
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BMJ Publishing Group 2023
Materias:	Cystic Fibrosis
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10231020/ https://www.ncbi.nlm.nih.gov/pubmed/37230763 http://dx.doi.org/10.1136/bmjresp-2022-001447

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