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Precision Editing as a Therapeutic Approach for β-Hemoglobinopathies

Beta-hemoglobinopathies are the most common genetic disorders worldwide, caused by a wide spectrum of mutations in the β-globin locus, and associated with morbidity and early mortality in case of patient non-adherence to supportive treatment. Allogeneic transplantation of hematopoietic stem cells (a...

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Detalles Bibliográficos
Autores principales:	Paschoudi, Kiriaki, Yannaki, Evangelia, Psatha, Nikoletta
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10253463/ https://www.ncbi.nlm.nih.gov/pubmed/37298481 http://dx.doi.org/10.3390/ijms24119527

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