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TRLS-01. FDA ANALYSIS OF EXPANDED ACCESS USE IN PEDIATRIC PATIENTS WITH CNS TUMORS FROM 2015 TO 2020
Few therapies are approved for children with central nervous system (CNS) tumors, and their prognosis is often poor. Expanded Access (EA) is a regulatory mechanism enabling patients with life-threatening or serious diseases to receive treatment with investigational drugs outside of clinical trials w...
Autores principales: | Duke, Elizabeth, Kormanik, Natasha, Barone, Amy, Chan, Mitchell, Antony, Ramya, Drezner, Nicole, Kluetz, Paul, Kim, Tamy, Singh, Harpreet, Pazdur, Richard, Donoghue, Martha |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Oxford University Press
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10260034/ http://dx.doi.org/10.1093/neuonc/noad073.304 |
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