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Overcoming the Challenges to Clinical Development of X-Linked Retinitis Pigmentosa Therapies: Proceedings of an Expert Panel
: X-linked retinitis pigmentosa (XLRP) is a rare inherited retinal disease manifesting as impaired night vision and peripheral vision loss that progresses to legal blindness. Although several trials of ocular gene therapy for XLRP have been conducted or are in progress, there is currently no approv...
Autores principales: | Birch, David G., Cheetham, Janet K., Daiger, Stephen P., Hoyng, Carel, Kay, Christine, MacDonald, Ian M., Pennesi, Mark E., Sullivan, Lori S. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
The Association for Research in Vision and Ophthalmology
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10270308/ https://www.ncbi.nlm.nih.gov/pubmed/37294701 http://dx.doi.org/10.1167/tvst.12.6.5 |
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