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AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype
Autores principales: | Boon, Nanda, Lu, Xuefei, Andriessen, Charlotte A., Moustakas, Ioannis, Buck, Thilo M., Freund, Christian, Arendzen, Christiaan H., Böhringer, Stefan, Boon, Camiel J.F., Mei, Hailiang, Wijnholds, Jan |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Elsevier
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10277829/ https://www.ncbi.nlm.nih.gov/pubmed/37315526 http://dx.doi.org/10.1016/j.stemcr.2023.05.008 |
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