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AAV-vectored base editor trans-splicing delivers dystrophin repair

Detalles Bibliográficos
Autores principales:	Li, Zhen, Gonçalves, Manuel A.F.V.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Society of Gene & Cell Therapy 2023
Materias:	Commentary
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10280080/ https://www.ncbi.nlm.nih.gov/pubmed/37346982 http://dx.doi.org/10.1016/j.omtn.2023.05.013

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