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Peripheral immune system modulates Purkinje cell degeneration in Niemann–Pick disease type C1

Niemann–Pick disease type C1 (NPC1) is a fatal lysosomal storage disorder characterized by progressive neuronal degeneration. Its key pathogenic events remain largely unknown. We have, herein, found that neonatal BM–derived cell transplantation can ameliorate Purkinje cell degeneration in NPC1 mice....

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Detalles Bibliográficos
Autores principales: Yasuda, Toru, Uchiyama, Toru, Watanabe, Nobuyuki, Ito, Noriko, Nakabayashi, Kazuhiko, Mochizuki, Hideki, Onodera, Masafumi
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Life Science Alliance LLC 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10300197/
https://www.ncbi.nlm.nih.gov/pubmed/37369603
http://dx.doi.org/10.26508/lsa.202201881