Economic Burden of Sanfilippo Syndrome in the United States

INTRODUCTION: Sanfilippo syndrome is a rare disease and fatal genetic disorder with no FDA-approved treatment in the United States (US), and no comprehensive assessment of economic disease burden is available. OBJECTIVES: To develop a model to estimate the economic burden associated with Sanfilippo...

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Detalles Bibliográficos
Autores principales: Ashby, Frederick, Park, Haesuk, Svensson, Mikael, Heldermon, Coy D.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Journal Experts 2023
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10312916/
https://www.ncbi.nlm.nih.gov/pubmed/37398464
http://dx.doi.org/10.21203/rs.3.rs-3001450/v4

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10312916/
https://www.ncbi.nlm.nih.gov/pubmed/37398464
http://dx.doi.org/10.21203/rs.3.rs-3001450/v4

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