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Growth patterns in patients with mucopolysaccharidosis VII

OBJECTIVE: This study assessed growth patterns in patients with mucopolysaccharidosis (MPS) VII before enzyme replacement therapy. METHODS: Height, weight, and body mass index (BMI) measurements and Z-scores from patients from three clinical studies were compared with those from CDC healthy populati...

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Detalles Bibliográficos
Autores principales:	Montaño, Adriana M., Różdżyńska-Świątkowska, Agnieszka, Jurecka, Agnieszka, Ramirez, Antonio Nino, Zhang, Lin, Marsden, Deborah, Wang, Raymond Y., Harmatz, Paul
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Elsevier 2023
Materias:	Research Paper
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10320588/ https://www.ncbi.nlm.nih.gov/pubmed/37415957 http://dx.doi.org/10.1016/j.ymgmr.2023.100987

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