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Targeting shared molecular etiologies to accelerate drug development for rare diseases

Rare diseases affect over 400 million people worldwide and less than 5% of rare diseases have an approved treatment. Fortunately, the number of underlying disease etiologies is far less than the number of diseases, because many rare diseases share a common molecular etiology. Moreover, many of these...

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Detalles Bibliográficos
Autores principales: Zanello, Galliano, Garrido‐Estepa, Macarena, Crespo, Ana, O'Connor, Daniel, Nabbout, Rima, Waters, Christina, Hall, Anthony, Taglialatela, Maurizio, Chan, Chun‐Hung, Pearce, David A, Dooms, Marc, Brooks, Philip John
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10331571/
https://www.ncbi.nlm.nih.gov/pubmed/37366158
http://dx.doi.org/10.15252/emmm.202217159