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Muscle Specific Promotors for Gene Therapy – A Comparative Study in Proliferating and Differentiated Cells
BACKGROUND: Depending on the therapy approach and disease background, the heterogeneity of muscular tissues complicates the development of targeted gene therapy, where either expression in all muscle types or restriction to only one muscle type is warranted. Muscle specificity can be achieved using...
Autores principales: | Dietz, Julienne, Jacobsen, Frank, Zhuge, Heidi, Daya, Nassam, Bigot, Anne, Zhang, Wenli, Ehrhardt, Anja, Vorgerd, Matthias, Ehrke-Schulz, Eric |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
IOS Press
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10357164/ https://www.ncbi.nlm.nih.gov/pubmed/37270809 http://dx.doi.org/10.3233/JND-221574 |
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