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Costs and health resource use in patients with X-linked myotubular myopathy: insights from US commercial claims

BACKGROUND: In X-linked myotubular myopathy (XLMTM), mutations in the MTM1 gene result in absence or dysfunction of myotubularin, a protein required for normal development, maintenance, and function of skeletal muscle. Extreme muscle weakness results in severe respiratory failure that is fatal for a...

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Detalles Bibliográficos
Autores principales:	Sacks, Naomi C, Healey, Bridget E, Cyr, Philip L, Slocomb, Theodore, James, Emma, Beggs, Alan H, Graham, Robert J
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Academy of Managed Care Pharmacy 2021
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10394177/ https://www.ncbi.nlm.nih.gov/pubmed/33843254 http://dx.doi.org/10.18553/jmcp.2021.20501

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