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Budget Impact Analysis of Eliglustat for the Treatment of Gaucher Disease Type 1 in the United States

BACKGROUND: Gaucher disease type 1 (GD1) is a rare, genetic, lysosomal storage disease with no cure. Current treatment options include intravenous (IV) enzyme replacement therapy ([ERT]; imiglucerase, velaglucerase alfa, or taliglucerase alfa) or oral substrate reduction therapy ([SRT]; eliglustat o...

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Detalles Bibliográficos
Autores principales:	Nalysnyk, Luba, Sugarman, Rebecca, Cele, Clifford, Uyei, Jennifer, Ward, Alexandra
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Academy of Managed Care Pharmacy 2018
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10397643/ https://www.ncbi.nlm.nih.gov/pubmed/30247105 http://dx.doi.org/10.18553/jmcp.2018.24.10.1002

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