Disease progression rates in ambulatory Duchenne muscular dystrophy by steroid type, patient age and functional status

AIMS: To examine benefits of corticosteroids for Duchenne muscular dystrophy (DMD) by age and disease progression. METHODS: Data from daily steroid users (placebo-treated) were pooled from four phase 2b/3 trials in DMD. Outcomes assessed overall and among subgroups included changes from baseline to...

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Detalles Bibliográficos
Autores principales: McDonald, Craig M, Marden, Jessica R, Shieh, Perry B, Wong, Brenda L, Lane, Henry, Zhang, Adina, Nguyen, Ha, Frean, Molly, Trifillis, Panayiota, Koladicz, Karyn, Signorovitch, James
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Becaris Publishing Ltd 2023
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10402754/
https://www.ncbi.nlm.nih.gov/pubmed/36749302
http://dx.doi.org/10.57264/cer-2022-0190

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