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25 years of maturation: A systematic review of RNAi in the clinic

The year 2023 marks the 25th anniversary of the discovery of RNAi. RNAi-based therapeutics enable sequence-specific gene knockdown by eliminating target RNA molecules through complementary base-pairing. A systematic review of published and ongoing clinical trials was performed. Web of Science, PubMe...

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Detalles Bibliográficos
Autores principales:	Corydon, Ida Juhl, Fabian-Jessing, Bjørn Kristensen, Jakobsen, Thomas Stax, Jørgensen, Asbjørn Cortnum, Jensen, Emilie Grarup, Askou, Anne Louise, Aagaard, Lars, Corydon, Thomas Juhl
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Society of Gene & Cell Therapy 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10424002/ https://www.ncbi.nlm.nih.gov/pubmed/37583575 http://dx.doi.org/10.1016/j.omtn.2023.07.018

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