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Burden and Treatment of Achondroplasia: A Systematic Literature Review

BACKGROUND: Achondroplasia is the most common form of skeletal dysplasia. Recent advances in therapeutic options have highlighted the need for understanding the burden and treatment landscape of the condition. This systematic literature review (SLR) aimed to identify health-related quality of life (...

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Detalles Bibliográficos
Autores principales:	Murton, Molly C., Drane, Emma L. A., Goff-Leggett, Danielle M., Shediac, Renée, O’Hara, Jamie, Irving, Melita, Butt, Thomas J.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Healthcare 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10427595/ https://www.ncbi.nlm.nih.gov/pubmed/37382866 http://dx.doi.org/10.1007/s12325-023-02549-3

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