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S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME

Detalles Bibliográficos
Autores principales: Hanna, Rabi, Frangoul, Haydar, Mckinney, Christopher, Pineiro, Luis, Mapara, Markus, Chang, Kai-Hsin, Jaskolka, Michael, Kim, Keunpyo, Rizk, Maha, Afonja, Olubunmi, Lawal, Adebayo, Walters, Mark
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Lippincott Williams & Wilkins 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10428233/
http://dx.doi.org/10.1097/01.HS9.0000967968.05170.e0