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S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME

Detalles Bibliográficos
Autores principales: Hanna, Rabi, Frangoul, Haydar, Mckinney, Christopher, Pineiro, Luis, Mapara, Markus, Chang, Kai-Hsin, Jaskolka, Michael, Kim, Keunpyo, Rizk, Maha, Afonja, Olubunmi, Lawal, Adebayo, Walters, Mark
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Lippincott Williams & Wilkins 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10428233/
http://dx.doi.org/10.1097/01.HS9.0000967968.05170.e0
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author Hanna, Rabi
Frangoul, Haydar
Mckinney, Christopher
Pineiro, Luis
Mapara, Markus
Chang, Kai-Hsin
Jaskolka, Michael
Kim, Keunpyo
Rizk, Maha
Afonja, Olubunmi
Lawal, Adebayo
Walters, Mark
author_facet Hanna, Rabi
Frangoul, Haydar
Mckinney, Christopher
Pineiro, Luis
Mapara, Markus
Chang, Kai-Hsin
Jaskolka, Michael
Kim, Keunpyo
Rizk, Maha
Afonja, Olubunmi
Lawal, Adebayo
Walters, Mark
author_sort Hanna, Rabi
collection PubMed
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spelling pubmed-104282332023-08-17 S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME Hanna, Rabi Frangoul, Haydar Mckinney, Christopher Pineiro, Luis Mapara, Markus Chang, Kai-Hsin Jaskolka, Michael Kim, Keunpyo Rizk, Maha Afonja, Olubunmi Lawal, Adebayo Walters, Mark Hemasphere Oral Sessions Lippincott Williams & Wilkins 2023-08-08 /pmc/articles/PMC10428233/ http://dx.doi.org/10.1097/01.HS9.0000967968.05170.e0 Text en Copyright © 2023 The Author(s). Published by Wolters Kluwer Health, Inc. https://creativecommons.org/licenses/by-nc-nd/4.0/This is an open access Abstract Book distributed under the Attribution-NonCommercial-NoDerivs (CC BY-NC-ND) (https://creativecommons.org/licenses/by-nc-nd/4.0/) which allows third parties to download the articles and share them with others as long as they credit the author and the Abstract Book, but they cannot change the content in any way or use them commercially.
spellingShingle Oral Sessions
Hanna, Rabi
Frangoul, Haydar
Mckinney, Christopher
Pineiro, Luis
Mapara, Markus
Chang, Kai-Hsin
Jaskolka, Michael
Kim, Keunpyo
Rizk, Maha
Afonja, Olubunmi
Lawal, Adebayo
Walters, Mark
S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
title S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
title_full S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
title_fullStr S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
title_full_unstemmed S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
title_short S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME
title_sort s264: edit-301 shows promising preliminary safety and efficacy results in the phase i/ii clinical trial (ruby) of patients with severe sickle cell disease using highly specific and efficient ascas12a enzyme
topic Oral Sessions
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10428233/
http://dx.doi.org/10.1097/01.HS9.0000967968.05170.e0
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