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P1392: INTERIM ANALYSIS OF FIRST IN HUMAN PHASE I-II CLINICAL TRIAL OF EX-VIVO GENE THERAPY FOR HURLER SYNDROME: AN UPDATE AT 3 YEAR FOLLOW-UP

Detalles Bibliográficos
Autores principales:	Tucci, Francesca, Consiglieri, Giulia, Filisetti, Chiara, De Pellegrin, Maurizio, Mellone, Renata, Fumagalli, Francesca, Darin, Silvia, Sarzana, Marina, Scarparo, Stefano, Ciotti, Francesca, Silvani, Paolo, Baldoli, Cristina, Pontesilli, Silvia, Parini, Rossella, la Marca, Giancarlo, Ciceri, Fabio, Naldini, Luigi, Aiuti, Alessandro, Gentner, Bernhard, Ester Bernardo, Maria
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2023
Materias:	Posters
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10430690/ http://dx.doi.org/10.1097/01.HS9.0000972456.19958.59

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