Cargando…
Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia B
Autores principales: | Schmidt, Manfred, Foster, Graham R., Coppens, Michiel, Thomsen, Hauke, Dolmetsch, Ricardo, Heijink, Liesbeth, Monahan, Paul E., Pipe, Steven W. |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
The American Society of Hematology
2023
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10463188/ https://www.ncbi.nlm.nih.gov/pubmed/37352263 http://dx.doi.org/10.1182/bloodadvances.2023009876 |
Ejemplares similares
-
Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapy
por: von Drygalski, Annette, et al.
Publicado: (2022) -
Efficient gene transduction in pigs and macaques with the engineered AAV vector AAV.GT5 for hemophilia B gene therapy
por: Kashiwakura, Yuji, et al.
Publicado: (2023) -
Development of an AAV DNA-based synthetic vector for the potential gene therapy of hemophilia in children
por: Shoti, Jakob, et al.
Publicado: (2022) -
An Observational Study from Long-Term AAV Re-administration in Two Hemophilia Dogs
por: Sun, Junjiang, et al.
Publicado: (2018) -
Preclinical assessment of an optimized AAV-FVIII vector in mice and non-human primates for the treatment of hemophilia A
por: Elkouby, Liron, et al.
Publicado: (2021)