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Gene Therapy in Hemophilia: A Transformational Patient Experience

Hemophilia is a bleeding disorder caused by a single absent/defective gene and characterized by a lack of functional clotting factors. People with hemophilia may experience joint damage, pain, and psychological impairments, all of which could contribute to reduced health-related quality of life (HRQ...

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Detalles Bibliográficos
Autores principales:	Rasul, Enayet, Hallock, Ryan, Hellmann, Magnus, Konduros, Jay, Pembroke, Luke, LeCleir, Gregory, Malacan, Jean, von Mackensen, Sylvia
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	SAGE Publications 2023
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10472832/ https://www.ncbi.nlm.nih.gov/pubmed/37663068 http://dx.doi.org/10.1177/23743735231193573

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