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Paving the way for future gene therapies: A case study of scientific spillover from delandistrogene moxeparvovec

Gene therapies have potential to improve outcomes of severe diseases after only a single administration. Novel therapies are continually being developed using knowledge gained from prior successes, a concept known as scientific spillover. Gene therapy advancement requires extensive development at ea...

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Detalles Bibliográficos
Autores principales:	Asher, Damon, Dai, Daisy, Klimchak, Alexa C., Sedita, Lauren E., Gooch, Katherine L., Rodino-Klapac, Louise
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	American Society of Gene & Cell Therapy 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10477757/ https://www.ncbi.nlm.nih.gov/pubmed/37674905 http://dx.doi.org/10.1016/j.omtm.2023.08.002

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