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An update on Becker muscular dystrophy

PURPOSE OF REVIEW: The purpose of this review is to summarise the recent developments in trial readiness, natural history studies, and interventional clinical trials for Becker muscular dystrophy (BMD). RECENT FINDINGS: As several treatment concepts have claimed to convert patients with Duchenne mus...

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Detalles Bibliográficos
Autores principales:	Straub, Volker, Guglieri, Michela
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2023
Materias:	MUSCULAR DISEASE: Edited by Benedikt Schoser
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10487383/ https://www.ncbi.nlm.nih.gov/pubmed/37591308 http://dx.doi.org/10.1097/WCO.0000000000001191

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