Applications and Research Advances in the Delivery of CRISPR/Cas9 Systems for the Treatment of Inherited Diseases

The rapid advancements in gene therapy have opened up new possibilities for treating genetic disorders, including Duchenne muscular dystrophy, thalassemia, cystic fibrosis, hemophilia, and familial hypercholesterolemia. The utilization of the clustered, regularly interspaced short palindromic repeat...

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Detalles Bibliográficos
Autores principales: Lu, Xinyue, Zhang, Miaomiao, Li, Ge, Zhang, Shixin, Zhang, Jingbo, Fu, Xiaoge, Sun, Fengying
Formato: Online Artículo Texto
Lenguaje:English
Publicado: MDPI 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10487642/
https://www.ncbi.nlm.nih.gov/pubmed/37686009
http://dx.doi.org/10.3390/ijms241713202

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10487642/
https://www.ncbi.nlm.nih.gov/pubmed/37686009
http://dx.doi.org/10.3390/ijms241713202

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