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Modeling the public health impact of voxelotor in the management of sickle cell disease in France

Sickle cell disease (SCD) is an inherited blood disorder in which sickle hemoglobin (HbS) polymerizes, leading to red blood cell sickling and chronic hemolytic anemia, vaso-occlusive crises, and end-organ damage associated with early mortality. Despite standard of care, patients with SCD still exper...

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Detalles Bibliográficos
Autores principales:	Galacteros, Frédéric, Ethgen, Olivier, Beillat, Maud
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Public Library of Science 2023
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10499253/ https://www.ncbi.nlm.nih.gov/pubmed/37703228 http://dx.doi.org/10.1371/journal.pone.0291211

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