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Hematopoietic cell transplantation and gene therapy for Diamond-Blackfan anemia: state of the art and science

Diamond-Blackfan anemia (DBA) is one of the most common inherited causes of bone marrow failure in children. DBA typically presents with isolated erythroid hypoplasia and anemia in infants. Congenital anomalies are seen in 50% of the patients. Over time, many patients experience panhematopoietic def...

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Detalles Bibliográficos
Autores principales: Bhoopalan, Senthil Velan, Suryaprakash, Shruthi, Sharma, Akshay, Wlodarski, Marcin W.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10518466/
https://www.ncbi.nlm.nih.gov/pubmed/37752993
http://dx.doi.org/10.3389/fonc.2023.1236038