Neurologic orphan diseases: Emerging innovations and role for genetic treatments

Orphan diseases are rare diseases that affect less than 200000 individuals within the United States. Most orphan diseases are of neurologic and genetic origin. With the current advances in technology, more funding has been devoted to developing therapeutic agents for patients with these conditions....

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Detalles Bibliográficos
Autores principales: Kioutchoukova, Ivelina P, Foster, Devon T, Thakkar, Rajvi N, Foreman, Marco A, Burgess, Brandon J, Toms, Rebecca M, Molina Valero, Eduardo E, Lucke-Wold, Brandon
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Baishideng Publishing Group Inc 2023
Materias:
Review
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10520757/
https://www.ncbi.nlm.nih.gov/pubmed/37767543
http://dx.doi.org/10.5493/wjem.v13.i4.59

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10520757/
https://www.ncbi.nlm.nih.gov/pubmed/37767543
http://dx.doi.org/10.5493/wjem.v13.i4.59

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