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Non-Viral Episomal Vector Mediates Efficient Gene Transfer of the β-Globin Gene into K562 and Human Haematopoietic Progenitor Cells

β-Thalassemia is a subgroup of inherited blood disorders associated with mild to severe anemia with few and limited conventional therapy options. Lately, lentiviral vector-based gene therapy has been successfully applied for disease treatment. However, the current development of non-viral episomal v...

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Detalles Bibliográficos
Autores principales:	Lazaris, Vassileios M., Simantirakis, Emmanouil, Stavrou, Eleana F., Verras, Meletios, Sgourou, Argyro, Keramida, Maria K., Vassilopoulos, George, Athanassiadou, Aglaia
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2023
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10530965/ https://www.ncbi.nlm.nih.gov/pubmed/37761914 http://dx.doi.org/10.3390/genes14091774

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