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Prevalence and cost of sickle cell disease in France: real-world analysis using data from the Echantillon Généraliste des Bénéficiaires

Sickle cell disease (SCD) is a genetic disorder of the hemoglobin resulting in chronic anemia, hemolysis, and vaso-occlusions. Its treatment mostly relies on hydroxycarbamide, transfusions, and stem cell transplantation. This study aimed at describing the epidemiology and management of SCD in adoles...

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Detalles Bibliográficos
Autores principales: Beillat, Maud, Durand-Zaleski, Isabelle, Pirenne, France, Bénard, Stève, Chillotti, Louis, Galacteros, Frédéric
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Frontiers Media S.A. 2023
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10552641/
https://www.ncbi.nlm.nih.gov/pubmed/37808997
http://dx.doi.org/10.3389/fpubh.2023.1215605