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Clinical trials in Charcot-Marie-Tooth disorders: a retrospective and preclinical assessment

OBJECTIVE: This study aimed to evaluate the progression of clinical and preclinical trials in Charcot-Marie-Tooth (CMT) disorders. BACKGROUND: CMT has historically been managed symptomatically and with genetic counseling. The evolution of molecular and pathologic understanding holds a therapeutic pr...

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Detalles Bibliográficos
Autores principales:	Nair, Malavika A., Niu, Zhiyv, Madigan, Nicholas N., Shin, Alexander Y., Brault, Jeffrey S., Staff, Nathan P., Klein, Christopher J.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Frontiers Media S.A. 2023
Materias:	Neurology
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10556688/ https://www.ncbi.nlm.nih.gov/pubmed/37808507 http://dx.doi.org/10.3389/fneur.2023.1251885

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